Agios submits Marketing Authorisation Application to European Medicines Agency for mitapivat for treatment of adults with Pyruvate Kinase Deficiency

Submission for this small molecule stimulator of pyruvate kinase follows recent submission to FDA for treatment of adults with this chronic, lifelong haemolytic anaemia for which there are no approved therapies, with current management based on blood transfusions and splenectomy

Biospace Inc.