Elamipretide receives orphan drug designation (ODD) from the European Medicines Agency for the treatment of Barth Syndrome
https://www.biospace.com/article/releases/stealth-biotherapeutics-receives-orphan-drug-designation-from-the-european-medicines-agency-for-elamipretide-for-the-treatment-of-barth-syndrome/
Source:
Biospace Inc.