FDA grants orphan drug designation for devimistat for biliary cancer

Devimistat is a lipoate analog, targeting the mitochondrial tricarboxylic acid cycle. It also has orphan status in the US for pancreatic cancer, acute myeloid leukaemia, myelodysplastic syndrome, peripheral T-cell lymphoma, soft tissue sarcoma, and Burkitt’s lymphoma.

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Biospace Inc.