Volanesorsen for treating familial chylomicronaemia syndrome – Final evaluation document
In DRAFT guidance, NICE recommends volanesorsen as an option for treating familial chylomicronaemia syndrome in adults with genetically confirmed familial chylomicronaemia syndrome who are at high risk of pancreatitis.
Source:
National Institute for Health and Care Excellence
SPS commentary:
It is recommended for use when response to diet and triglyceride-lowering therapy has been inadequate, and only if the company provides volanesorsen according to the commercial arrangement.